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Alphabetical List of Disease Areas
A B C
D E F
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M N O
P Q R
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AAT Congenital Deficiency
Achondroplasia
Acromegaly
Acute Disseminated Encephalomyelitis
Acute Lymphoblastic Leukemia
Acute Myeloid Leukemia Adult
Acute Radiation Syndrome
Addisons Disease
Adenosine Deaminase Deficiency
Adrenal Hyperplasia, Congenital
Adrenocortical Carcinoma (ACC)
Adrenoleukodystrophy X-Linked
Adult Growth Hormone Deficiency
AL Amyloidosis
Alagille Syndrome
Alexander Disease
Alopecia
Alpha 1 Antitrypsin Deficiency
Alpha Mannosidosis
Alport Syndrome
Altitude Sickness
Amoebiasis
Amyloid Neuropathy
Amyloidosis
Amyotrophic Lateral Sclerosis (ALS)
Anaemia in Chronic Kidney Disease (CKD) (Dialysis)
Anaemia, AIDS Related
Anaemia, Aplastic
Anaemia, Haemolytic
Anaemia, Megaloblastic
Anaemia, Other
Anal Dysplasia
Anaphylaxis
Aniridia
Anthrax Prophylaxis
Anthrax Treatment
Anti Thrombin III Deficiency
Apnoea of Prematurity
Arrhythmia, Ventricular
Arteriovenous Fistula
Arthritis, General
Arthritis, Rheumatoid
Aspergillosis Infections
Asthenia
Ataxia Telangiectasia
Autoimmune Hepatitis
Autosomal Recessive Polycystic Kidney Disease
B Cell Lymphomas
Bacteraemia
Bacterial Meningitis
Basal Cell Carcinoma (BCC)
Becker Muscular Dystrophy
Behcets Syndrome
Benign Hyperphenylalaninemia
Benign Recurrent Intrahepatic Cholestasis 1
Biliary Cancer
Bladder Cancer
Blepharospasm
Blood Substitution
Bone Cancer (Osteosarcoma)
Bone Marrow Transplantation
Botulism Treatment
Bowel Clearance
Brain Cancer
Brain Metastases
Brain Tumor Adult
Bronchiectasis Oligospermia
Bronchiolitis Obliterans
Bronchitis, Chronic
Bronchopulmonary Dysplasia
Buergers Disease
Bullous Pemphigoid
Cachexia (Wasting), AIDS Related
Cancer Related Bone Loss
Candidiasis Familial Chronic Mucocutaneous Autosomal Recessive
Carcinoid Syndrome
Cardiogenic Shock
Cardiopulmonary Bypass Surgery
Carnitine Transporter Deficiency
Castleman Disease
Cataract And Congenital Ichthyosis
Cerebral Oedema
Cerebral Palsy
Cerebrotendinous Xanthomatosis (CTX)
Cervical Cancer
Cervical Dystonia
Cestodes (Tapeworm) Infections
Chagas Disease
Charcot Marie Tooth Disease
Chemotherapy Induced Hyperuricaemia
Childhood Onset Schizophrenia
Cholelithiasis
Cholestasis
Cholesteryl Ester Storage Disease
Choroideremia
Chronic Fatigue Syndrome
Chronic Granulomatous Disease
Chronic Inflammatory Demyelinating Polyneuropathy (CIDP)
Chronic Kidney Disease (CKD)
Chronic Lymphocytic Leukemia
Churg Strauss Syndrome
Cias1 Associated Periodic Syndromes (CAPS)
Circadian Rhythm Sleep Disorders
Clostridium Difficile Associated Diarrhoea (CDAD)
CMV Infection Prophylaxis
CMV Infection, AIDS Related
CMV Infections
Cockayne Syndrome
Cold Agglutinin Disease
Colorectal Cancer
Congenital Adrenal Hyperplasia
Congenital Cytomegalovirus
Congenital Hepatic Fibrosis
Congenital Human Immunodeficiency Virus
Congenital Muscular Dystrophy
Congenital Sucrase Isomaltase Deficiency (CSID)
Congestive Heart Failure (CHF)
Conjunctivitis Ligneous
Conjunctivitis, Allergic
Coronary Artery Bypass Graft (CABG)
Crigler Najjar Syndrome
Crohns Disease
Cryptosporidiosis
Cushings Syndrome
Cutaneous T Cell Lymphoma
Cystic Fibrosis (CF)
Cystinuria
Cystitis
A B C
D E F
G H I
J K L
M N O
P Q R
S T U
V W X Y Z
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Dementia, Frontotemporal
Dengue Fever Treatment
Diarrhoea
Diffuse Systemic Sclerosis
Dilated Cardiomyopathy
Dravet Syndrome
Drug Toxicity
Duchenne Muscular Dystrophy
Dupuytrens Contracture
Dyskinesia Drug Induced
Ebola Haemorrhagic Fever (EHF)
Ebola Virus Disease
Eclampsia
Ehlers Danlos Syndrome
Emesis
Emphysema
Endophthalmitis
Enterovirus Antenatal Infection
Eosinophilic Oesophagitis
Epidermolysis Bullosa (EB)
Epilepsy
Erythromelalgia Primary
Esophageal Ulcer
Essential Thrombocythemia
Ewings Sarcoma
Fabry Disease
Facioscapulohumeral Muscular Dystrophy (FSHD)
Facioscapulohumeral Muscular Dystrophy 1A
Factor X Deficiency
Factor XI Deficiency
Factor XIII Deficiency
Faecal Incontinence
Fallopian Tube Cancer
Familial Adenomatous Polyposis (FAP)
Familial Colorectal Cancer
Familial Lipoprotein Lipase Deficiency
Familial Mediterranean Fever
Familial Pulmonary Arterial Hypertension Leucopenia And Atrial Septal Defect
Familial Transthyretin Amyloidosis
Fibrodysplasia Ossificans Progressiva
Focal Segmental Glomerulosclerosis (FSGS)
Follicular Lymphoma
Fragile X Syndrome
Friedreich Ataxia
A B C
D E F
G H I
J K L
M N O
P Q R
S T U
V W X Y Z
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Gallstones
Gastro Intestinal Adenocarcinoma
Gastro Intestinal Fistula
Gastro Intestinal Stromal Tumours (GIST)
Gaucher Disease
Germ Cell Tumour
Gi Spasm
Giardiasis
Glaucoma
Glioblastoma Multiforme
Glioma
Globoid Cell Leukodystrophy (GLD)
Glomerulonephritis
Glucose Transporter Type 1 Deficiency Syndrome
Glycogen Storage Disease Type 2 (Pompe Disease)
Gout
Graft vs Host Disease (Gvhd)
Gram Negative Infections
Granulomatosis with Polyangiitis
Graves Disease
Growth Hormone Deficiency
Guillain Barre Syndrome
Haemolytic Uremic Syndrome
Haemorrhagic Fever with Renal Syndrome (HFRS) Prophylaxis
Heart Transplantation
Hemophagocytic Lymphohistiocytosis
Hemophilia A Congenital
Hemophilia B
Hepatic Encephalopathy
Hepatitis B Prophylaxis
Hepatitis B Treatment
Hepatitis C Prophylaxis
Hepatitis C Treatment
Hepatitis D Treatment
Hepatoma, Liver Cancer
Hereditary Angioedema
Hereditary Cerebral Hemorrhage with Amyloidosis
Hidradenitis Suppurativa
HIV Associated Nephropathy
Hodgkin Lymphoma
Homocystinuria
Homozygous Familial Hypercholesterolemia
Hunter Syndrome (Mucopolysaccharidosis II Or MPS II)
Huntington Disease
Hurlers Syndrome (Mucopolysaccharidosis I Or MPS I)
Hutchinson Gilford Progeria Syndrome
Hyperammonaemia
Hypercalcaemia
Hyperimmunoglobulinemia D Syndrome (HIDS)
Hyperinsulinemic Hypoglycemia Familial 2
Hyperinsulinemic Hypoglycemia Familial 2 & 3
Hyperlipoproteinemia Type 1
Hyperoxaluria
Hyperparathyroidism
Hyperphosphataemia
Hyperprolactinaemia
Hypersomnia
Hypertrophic Cardiomyopathy
Hyperuricaemia
Hypoglycaemia
Hypogonadism
Hypolipoproteinemia
Hypoparathyroidism
Hypophosphatasia
Hypophosphatemic Rickets
Hypotension
Hypoxia
Idiopathic Pulmonary Fibrosis
Idiopathic Thrombocytopenic Purpura
Iga Nephropathy
Immune Thrombocytopenia
Immunoglobulin Deficiency
Inclusion Body Myopathy 2
Inclusion Body Myositis
Infantile Spasms Broad Thumbs
Iron Poisoning
A B C
D E F
G H I
J K L
M N O
P Q R
S T U
V W X Y Z
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Kaposis Sarcoma
Keratitis Hereditary
Keratoconus
Kidney Stones
Kidney Transplantation
Krabbes Disease
Lambert Eaton Myasthenic Syndrome
Large B Cell Diffuse Lymphoma
Late Acute Graft Versus Host Disease
Leber Congenital Amaurosis
Leber Congenital Amaurosis Type 2
Leber Hereditary Optic Neuropathy
Leigh Syndrome
Leishmaniasis Treatment
Lennox Gastaut Syndrome
Leprosy
Lesch Nyhan Syndrome
Leukaemia, Acute
Leukaemia, Acute Lymphocytic (ALL)
Leukaemia, Acute Myeloid (AML)
Leukaemia, Chronic Lymphocytic (CLL)
Leukaemia, Chronic Myeloid (CML)
Leukaemia, Hairy Cell (HCL)
Leukaemia, T Cell
Limb Girdle Muscular Dystrophy
Lipodystrophy
Liposomal Acid Lipase Deficiency
Liver Transplantation
Long QT Syndrome 1
Lung Transplantation
Lymphangioleiomyomatosis
A B C
D E F
G H I
J K L
M N O
P Q R
S T U
V W X Y Z
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Malignant Ascites
Malignant Mesothelioma
Mantle Cell Lymphoma
Maple Syrup Urine Disease
Marburg Haemorrhagic Fever
Marfan Syndrome
Maroteaux Lamy Disease (Mucopolysaccharidosis VI Or MPS VI)
Mastocytosis
Melanoma
Meningitis, Cryptococcal AIDS Related
Mesothelioma
Metachromatic Leukodystrophy (MLD)
Methaemoglobinaemia
Methicillin Resistant Staphylococcus Aureus (MRSA) Infections
Methylmalonic Acidaemia (MMA)
Mitochondrial Complex Deficiency I V
Mitochondrial Disease
Mitochondrial Encephalopathy, Lactic Acidosis, And Stroke Like Episodes (MELAS)
Mitochondrial Oxidative Phosphorylation Disorders
Molybdenum Cofactor Deficiency
Morquio Syndrome (Mucopolysaccharidosis IV Or MPS IV)
Mucocutaneous Dryness
Mucopolysaccharidosis Type I
Mucopolysaccharidosis Type II
Mucopolysaccharidosis Type IIIA
Mucopolysaccharidosis Type IIIB
Mucopolysaccharidosis Type VII
Multifocal Motor Neuropathy (MMN)
Multiple Myeloma
Multiple Pterygium Syndrome X-Linked
Muscle Spasticity
Muscular Dystrophy
Musculoskeletal Inflammation
Myasthenia Gravis
Mycobacterium Avium Complex Infections
Mycosis Fungoides
Myelodysplastic Syndromes
Myelofibrosis
Myocardial Infarction, Acute (AMI)
Myotonic Dystrophy
Narcolepsy
Necrotizing Enterocolitis
Necrotizing Fasciitis
Nematode (Roundworm) Infections
Neonatal Ovarian Cyst
Neoplastic Meningitis
Nephropathic Cystinosis
Nephrotic Syndrome
Neuroblastoma
Neuroendocrine Tumour
Neuromyelitis Optica Spectrum Disorder
Neuronal Ceroid Lipofuscinoses
Neutropaenia
Neutropenia And Thrombocytopenia And Anemia
Niemann Pick Disease Type C1
Noma
Non Hodgkin Lymphoma (NHL)
Non Hodgkin Lymphoma Childhood
Non Small Cell Lung Cancer (NSCLC)
Non Tuberculosis Mycobacterial Lung Disease and Cystic Fibrosis
Narcolepsy
Necrotizing Enterocolitis
Necrotizing Fasciitis
Nematode (Roundworm) Infections
Neonatal Ovarian Cyst
Neoplastic Meningitis
Nephropathic Cystinosis
Nephrotic Syndrome
Neuroblastoma
Neuroendocrine Tumour
Neuromyelitis Optica Spectrum Disorder
Neuronal Ceroid Lipofuscinoses
Neutropaenia
Neutropenia And Thrombocytopenia And Anemia
Niemann Pick Disease Type C1
Noma
Non Hodgkin Lymphoma (NHL)
Non Hodgkin Lymphoma Childhood
Non Small Cell Lung Cancer (NSCLC)
Non Tuberculosis Mycobacterial Lung Disease and Cystic Fibrosis
Oesophageal Cancer
Oesophageal Varices
Optic Neuritis
Optic Neuromyelitis
Optic Neuropathy Anterior Ischemic
Organ Rejection
Organic Acidemia
Osteoporosis
Ovarian Cancer
A B C
D E F
G H I
J K L
M N O
P Q R
S T U
V W X Y Z
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Pachyonychia Congenita
Pagets Disease
Pancreatic Cancer
Pancreatic Islet Transplantation
Pancreatitis
Pantothenate Kinase Associated Neurodegeneration
Panuveitis
Parkinson Disease
Paroxysmal Nocturnal Haemoglobinuria (PNH)
Patent Ductus Arteriosus
Pcdh19 Epilepsy
Pediatric Crohns Disease
Pediatric Ulcerative Colitis
Pemphigus Vulgaris
Peripheral Neuropathy
Peripheral T Cell Lymphoma
Peripheral Vascular Disease (PVD)
Pertussis
Peyronies Disease
Phenylketonuria (PKU)
Plague Treatment
Pleural Effusion
Pneumocystis Jiroveci (Pneumocystis Carinii) Infections
Polio Prophylaxis
Polyarthritis Systemic
Polycystic Kidney Disease (PKD)
Polycystic Liver Disease
Polycystic Ovarian Syndrome
Polycythaemia Vera
Polymyositis
Polymyositis and Dermatomyositis
Porphyria
Post Transplant Lymphoproliferative Disease
Postherpetic Neuralgia
Pouchitis
Prader Willi Syndrome
Pre Eclampsia
Precocious Puberty
Primary Biliary Cirrhosis (PBC)
Primary Sclerosing Cholangitis
Progressive Multifocal Leukoencephalopathy (PML)
Progressive Supranuclear Palsy
Prostate Cancer
Proteus Syndrome
Pruritus
Pseudomonas Infections
Pulmonary Alveolar Proteinosis
Pulmonary Fibrosis, Idiopathic
Pulmonary Hypertension
Pyruvate Kinase Deficiency
Rabies
Renal Cell Carcinoma (RCC)
Renal Osteodystrophy
Respiratory Distress Syndrome (RDS)
Retinal Detachment
Retinal Telangiectasia Hypogammaglobulinemia
Retinal Vein Occlusion
Retinitis Pigmentosa
Retinoblastoma
Retinopathy of Prematurity
Rett Syndrome
Rosacea
RSV Infections
A B C
D E F
G H I
J K L
M N O
P Q R
S T U
V W X Y Z
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Sanfilippo Syndrome (Mucopolysaccharidosis III or MPS III)
Sarcoidosis
Schizophrenia
Scleroderma
Sclerosing Cholangitis
Severe Combined Immunodeficiency Disease (SCID)
Short Bowel Syndrome
Sickle Cell Anemia
Sjogrens Syndrome
Skin Cancer, Non Melanoma
Slys Syndrome (Mucopolysaccharidosis VII Or MPS VII)
Small Cell Lung Cancer (SCLC)
Smallpox
Smallpox Prophylaxis
Soft Tissue Sarcoma
Solid Tumour Indications
Sphingolipidosis
Spinal Cord Injury
Spinal Muscular Atrophy
Spinocerebellar Ataxia
Squamous Cell Carcinoma of The Head And Neck
Staphylococcal Infections
Stargardt Disease
Status Epilepticus
Stiff Person Syndrome
Stomach Carcinoma
Stomatitis (Mouth Ulcers)
Strabismus (Crossed Eyes)
Stroke, Acute
Subarachnoid Haemorrhage
Surgical Adhesions
Systemic Lupus Erythematosus (SLE)
T Cell Lymphoma 1A
Tay Sachs and Sandhoffs Disease
Testicular Cancer
Testosterone Deficiency
Thalassaemia
Thromboangiitis Obliterans
Thrombocythaemia
Thrombocytopaenia
Thrombosis
Thrombosis, Deep Vein (DVT)
Thrombotic Thrombocytopenic Purpura Congenital
Thyroid Cancer
Tourette Syndrome (Pediatric)
Tourettes Syndrome
Toxoplasmosis
Toxoplasmosis, AIDS Related
Traumatic Brain Injury
Trematode (Fluke) Infections
Trypanosomiasis
Tuberous Sclerosis
Tumor Necrosis Factor Receptor Associated Periodic Syndrome (TRAPS)
Turners Syndrome
Type 1 Plasminogen Deficiency
Tyrosinaemia
Ulcerative Colitis
Ulcers, Chronic Skin
Ulcers, Corneal
Upper Respiratory Tract Infections
Urea Cycle Disorders
Urinary Calculi
Urticaria
Usher Syndrome
Uterine Cancer
Uveitis
A B C
D E F
G H I
J K L
M N O
P Q R
S T U
V W X Y Z
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Varicella Infections
Vasculitis
Veno Occlusive Disease (VOD)
Von Hippel Lindau Disease
Von Willebrand Disease (VWD)
Vulvar Dysplasia
Waldenstrom Macroglobulinemia
Wegeners Granulomatosis
West Nile Virus (WNV) Disease
Whooping Cough
Wilson Disease
Wiskott Aldrich Syndrome
Wolmans Disease
X-Linked Hypohidrotic Ectodermal Dysplasia
About
Team
Development Blog
White Papers
Contact Us
Services
Market Access and Forecasting
Data Management and Analytics
Global Pricing and Reimbursement
HEOR
Marketing and Messaging Analytics
Stakeholder Advisory Boards
Products
Indications
Therapeutics
BUSINESS DEVELOPMENT
RareValue
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RareValue Example
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