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PERSPECTIVES ON BIOPHARMA TRENDS

Therapeutic Development: ALK-001

1/6/2017

 
ALK-001 is a drug candidate being developed by Alkeus Pharmaceuticals for the treatment of Stargardt Disease (STGD1). Vitamin A dimers are the primary cause of vision loss associated with Stargardt Disease due to retinal toxicity. ALK-001 is a modified form of vitamin A that prevents aggregation into dimers.
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  • About
    • Team
    • Development Blog
    • White Papers
    • Contact Us
  • Services
    • Market Access and Forecasting
    • Data Management and Analytics
    • Global Pricing and Reimbursement
    • HEOR
    • Marketing and Messaging Analytics
    • Stakeholder Advisory Boards
  • Products
    • Indications
    • Therapeutics
  • BUSINESS DEVELOPMENT
    • RareValue >
      • RareValue Example
    • Out-License
    • On-Site Workshop